Search for Clinical Trial Results
Osteochondrodysplasias - 25 Studies Found
Status | Study |
Active, not recruiting |
Study Name: Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAPLE Study) Condition:
Date: 2014-08-01 |
Completed |
Study Name: Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease Condition:
Date: 2012-10-12 Interventions: Other: Enzyme testing Leukocyte activity measurement of Arylsulfatase B and N acetyl galactosamine 6 sul |
Recruiting |
Study Name: A Multicenter, Multinational, Observational Morquio A Registry Study (MARS) Condition:
Interventions: Drug: Vimizim® (elosulfase alfa) Recombinant human N acetylgalactosamine 6 sulfatase (rhGALNS) |
Terminated |
Study Name: Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics Condition:
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Completed |
Study Name: Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Condition:
|
Recruiting |
Study Name: Longitudinal Studies of Brain Structure and Function in MPS Disorders Condition:
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Completed |
Study Name: A Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IVA Condition: MPS IV A Date: 2009-04-10 Interventions: Drug: BMN 110 Subjects will receive a weekly 4- to 5-hour |
Completed |
Study Name: A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Condition: MPS IV A Date: 2011-01-10 Interventions:
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Approved for marketing |
Study Name: BMN 110 US Expanded Access Program Condition:
Date: 2013-05-15 Interventions: Drug: BMN 110 |
Enrolling by invitation |
Study Name: Immunodeficiency in Cartilage-hair Hypoplasia: Sub-project on Safety of Vaccination Against Chickenpox Condition: Cartilage-hair Hypoplasia Date: 2015-02-10 Interventions: Biological: Varilrix Vaccination against varicella in selected cartilage-hair hypoplasia patients |