Search for Clinical Trial Results
Familial Transthyretin Amyloidosis - 25 Studies Found
Status | Study |
Completed |
Study Name: Safety, Efficacy and Pharmacokinetics of Doxycycline Plus Tauroursodeoxycholic Acid in Transthyretin Amyloidosis Condition: Transthyretin Amyloidosis Date: 2010-07-27 Interventions: Drug: Doxycycline + Tauroursodeoxycholic acid doxycycline 100 mg twice a day for 12 months; tauroursodeo |
Completed |
Study Name: Study of SOM0226 in Familial Amyloid Polyneuropathy Condition: Familial Amyloid Polyneuropathy (FAP) Date: 2014-07-09 Interventions: Drug: SOM0226 Oral |
Completed |
Study Name: The Effect Of Tafamidis For The Transthyretin Amyloid Polyneuropathy Patients With V30M Or Non-V30M Transthyretin Condition: Transthyretin Familial Amyloid Polyneuropathy Date: 2011-09-13 Interventions: Drug: tafamidis tafamidis meglumine 20 mg QD Other N |
Completed |
Study Name: An Extension of Study Fx-005 Evaluating Long-Term Safety And Clinical Outcomes Of Fx-1006A In Patients With Transthyretin Amyloid Polyneuropathy Condition:
Date: 2008-11-13 Interventions: Drug: Fx-1006A Fx-1006A 20mg soft gelatin capsule administered orally once daily (at the same time each |
Completed |
Study Name: Safety and Efficacy Study of Fx-1006A in Patients With Familial Amyloidosis Condition: Familial Amyloid Polyneuropathy Date: 2006-12-06 Interventions:
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Completed |
Study Name: The Effect of Diflunisal on Familial Transthyretin Amyloidosis Condition: Amyloidosis Date: 2011-09-09 Interventions: Drug: Diflunisal Film-coated tablet, 250 mg twice daily, orally for approximately 2 years |
Active, not recruiting |
Study Name: Efficacy and Safety of IONIS-TTR Rx in Familial Amyloid Polyneuropathy Condition:
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Enrolling by invitation |
Study Name: Open-Label Extension Assessing Long Term Safety and Efficacy of IONIS-TTR Rx in Familial Amyloid Polyneuropathy (FAP) Condition:
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Recruiting |
Study Name: Transthyretin-Associated Amyloidoses Outcome Survey (THAOS) Condition:
Date: 2008-02-25 Interventions: Other: None. Observational Study. |