Search for Clinical Trial Results
Mucopolysaccharidosis Type IV - 47 Studies Found
Status | Study |
Terminated |
Study Name: Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome Condition:
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Terminated |
Study Name: A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome) Condition:
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Withdrawn |
Study Name: Dynamic Gait Analysis in Children With Mucopolysaccharidosis Type IVa Condition:
Date: 2014-05-28 |
Completed |
Study Name: Screening an Orthopedic Population for Mildly-affected Individuals With Morquio Syndrome A and Maroteaux-Lamy Syndrome Condition:
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Approved for marketing |
Study Name: BMN 110 US Expanded Access Program Condition:
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