Clinical Trial: Application of Miglustat in Patients With Niemann-Pick Type C
Study Status: Completed
Recruit Status: Completed
Study Type: Interventional
Official Title: Application of Miglustat in Patients With Niemann-Pick Type C
Brief Summary: To evaluate the changes in cognitive function after miglustat treatment in Niemann-Pick type C patients.
Detailed Summary: Patients with Niemann-Pick C disease will be treated with Miglutat 200mg tid. Neurologic evaluation and safety will be monitored periodically.
Sponsor: National Taiwan University Hospital
Current Primary Outcome: Swallowing [ Time Frame: 12th month ]
Original Primary Outcome: Same as current
Current Secondary Outcome: Mental [ Time Frame: 12th month ]
Original Secondary Outcome: Same as current
Information By: National Taiwan University Hospital
Dates:
Date Received: January 2, 2013
Date Started: January 2008
Date Completion:
Last Updated: January 3, 2013
Last Verified: November 2012