Clinical Trial: A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)

Study Status: Terminated
Recruit Status: Terminated
Study Type: Observational

Official Title: A Multicenter, Multinational, Longitudinal Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)

Brief Summary: This multicenter, multinational, longitudinal study will quantify endurance and respiratory function in subjects diagnosed with MPS IVA and will better characterize the spectrum of symptoms and biochemical abnormalities in MPS IVA disease over time.

Detailed Summary:
Sponsor: BioMarin Pharmaceutical

Current Primary Outcome:

  • Endurance [ Time Frame: Study Visit ]
  • Respiratory Function [ Time Frame: Study Visit ]


Original Primary Outcome: Same as current

Current Secondary Outcome:

Original Secondary Outcome:

Information By: BioMarin Pharmaceutical

Dates:
Date Received: November 6, 2008
Date Started: October 2008
Date Completion:
Last Updated: December 5, 2014
Last Verified: December 2014