Clinical Trial: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB
Study Status: Completed
Recruit Status: Completed
Study Type: Observational
Official Title: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB
Brief Summary: The objective is to perform a retrospective chart review to generate data to evaluate the clinical characteristics and course of disease progression of MPS IIIB.
Detailed Summary:
Sponsor: Alexion Pharmaceuticals
Current Primary Outcome: Evaluation of disease presentation and the course of disease progression including the end stage of the disease in patients with MPS IIIB, assessed from medical history data obtained by retrospective chart review of deceased patients. [ Time Frame: N/A as this is a retrospective chart review of deceased patients ]
Original Primary Outcome: Evaluation of disease presentation and the course of disease progression including the end stage of the disease in patients with MPS IIIB, assessed from medical history data obtained by retrospective chart review of deceased patients. [ Time Frame: N/A as this is a retrospective chart review of deceased patients ]
Current Secondary Outcome:
Original Secondary Outcome:
Information By: Alexion Pharmaceuticals
Dates:
Date Received: November 3, 2014
Date Started: July 2013
Date Completion:
Last Updated: February 2, 2017
Last Verified: February 2017