Clinical Trial: Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I
Study Status: Enrolling by invitation
Recruit Status: Enrolling by invitation
Study Type: Interventional
Official Title: An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I
Brief Summary: This is a five-year extension study of the pilot study, "Intrathecal Enzyme Replacement for Cognitive Decline in MPS I". Participants must have completed the pilot study to participate in this study.
Detailed Summary:
Sponsor: agnes chen
Current Primary Outcome: Hopkins Verbal Learning Test [ Time Frame: 5 years ]
Original Primary Outcome: Same as current
Current Secondary Outcome:
Original Secondary Outcome:
Information By: Los Angeles Biomedical Research Institute
Dates:
Date Received: September 3, 2014
Date Started: May 2014
Date Completion: June 2020
Last Updated: May 5, 2017
Last Verified: May 2017