Clinical Trial: Muscle Response to Enzyme Replacement Therapy in Pompe Disease

Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Observational

Official Title: Muscle Response to Enzyme Replacement Therapy in Pompe Disease

Brief Summary: This study is to study the response of muscle cells from Pompe disease after enzyme replacement therapy

Detailed Summary:
Sponsor: National Taiwan University Hospital

Current Primary Outcome: all morphology changes improvement [ Time Frame: 6 months ]

Original Primary Outcome:

Current Secondary Outcome:

Original Secondary Outcome:

Information By: National Taiwan University Hospital

Dates:
Date Received: July 9, 2008
Date Started: January 2007
Date Completion: December 2019
Last Updated: March 21, 2015
Last Verified: March 2015