Clinical Trial: Miglustat on Gaucher Disease Type IIIB
Study Status: Recruiting
Recruit Status: Recruiting
Study Type: Interventional
Official Title: Evaluation of Combination Therapy With Miglustat and Enzyme Replacement Therapy on Gaucher Disease Type IIIB
Brief Summary: evaluate the combination therapy with Miglustat and enzyme replacement therapy (ERT) on Gaucher disease
Detailed Summary: understand if Miglustat (glucosylceramide synthase inhibitor) could improve neuropathy in patients with Gaucher disease
Sponsor: National Taiwan University Hospital
Current Primary Outcome: Improve in Purdue Pegboard test speed [ Time Frame: 24 months ]
Original Primary Outcome: Same as current
Current Secondary Outcome:
Original Secondary Outcome:
Information By: National Taiwan University Hospital
Dates:
Date Received: August 6, 2015
Date Started: July 2015
Date Completion: July 2018
Last Updated: April 13, 2017
Last Verified: July 2016